leukodystrophy
leukodystrophy
UK Invests Big in Advanced Therapy Manufacturing!
BIOT
The U.K. is bullish on advanced therapy manufacturing! 💪💰 £520 million investment fosters innovation and retains gene therapies. 🚀🌍
SynaptixBio Receives FDA ODD for Leukodystrophy Treatment
BIOT
📰 Rare disease specialist SynaptixBio Ltd receives FDA ODD for TUBB4A leukodystrophy, allowing research on therapy for isolated hypomyelination. 💊💡✨
